Utilizing mTOR Inhibitors to Stabilize Intermediate Filaments in Epidermolysis Bullosa

Time: 12:00 pm
day: Day Two Clinical Track AM


  • Examining the role of mechanistic target of rapamycin (mTOR) in Epidermolysis Bullosa to unveil the rationale behind mTOR inhibition
  • Exploring mTOR inhibitor’s ability to degrade and remove mutant keratins through stimulation of autophagy
  • The promise of BM-3103 in orphan diseases as a novel approach to treating unmet needs